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Targeted Peptide-Mediated Delivery of Antisense Oligonucleotides to SMA Cells for SMN2 Gene Splicing Correction Full article

Journal Scientia Pharmaceutica
ISSN: 2218-0532
Output data Year: 2025, Volume: 93, Number: 3, Article number : 38, Pages count : 13 DOI: 10.3390/scipharm93030038
Authors Maretina Marianna 1 , Egorova Anna 1 , Il’ina Arina 1 , Krylova Nadezhda 1 , Donnikov Maxim 2 , Glotov Oleg 1 , Kiselev Anton 1
Affiliations
1 Department of Genomic Medicine named after V.S. Baranov, D.O. Ott Research Institute of Obstetrics, Gynecology and Reproductology, Mendeleevskaya Line 3, 199034 Saint-Petersburg, Russia
2 Department of Children’s Diseases, Medical Institute of Surgut State University, 628400 Surgut, Russia

Funding (1)

1 Фонд научно-технологического развития Ханты-Мансийского автономного округа – Югры 2023-561-05/2023
Cite: Maretina M. , Egorova A. , Il’ina A. , Krylova N. , Donnikov M. , Glotov O. , Kiselev A.
Targeted Peptide-Mediated Delivery of Antisense Oligonucleotides to SMA Cells for SMN2 Gene Splicing Correction
Scientia Pharmaceutica. 2025. V.93. N3. 38 :1-13. DOI: 10.3390/scipharm93030038
Identifiers: No identifiers
Citing: Пока нет цитирований
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